California-based gene therapy company 4D Molecular Therapeutics (4DMT), which is focused on adeno-associated virus (AAV) gene therapy vector discovery and product development, has raised $70 million through a Series C financing round. The Series C financing round was led by Viking Global Investors. It also saw participation from new investors such as Amzak Health, Casdin […]
Vertex Pharmaceuticals is set to launch its cystic fibrosis drug KALYDECO (ivacaftor) in New Zealand, which will be available to eligible patients from next month. The US biopharma company said that clinicians can apply for patient access using the exceptional circumstances framework under the Pharmaceutical Management Agency (PHARMAC). Ludovic Fenaux – Senior Vice President of […]
Continue reading …Allergan has agreed to sell IL-23 inhibitor brazikumab to AstraZeneca and gastrointestinal medication Zenpep (pancrelipase) to Nestle in separate agreements, as per the latest pharma acquisition news. Financial details of the two deals have not been disclosed. The divestments are being taken up in an effort to wrap up the $63 billion AbbVie acquisition of […]
Continue reading …Boston-based biopharma company Proteostasis Therapeutics has dosed the first patient in a phase 2 clinical trial of its cystic fibrosis transmembrane conductance regulator (CFTR) modulator combinations in F508del homozygous and heterozygous cystic fibrosis patients. The 28-day phase 2 study has been initiated after getting positive results from the 14-day phase 1 clinical studies of the […]
Continue reading …Synspira has been given the orphan designation status by the US Food and Drug Administration (FDA) for poly (acetyl, arginyl) glucosamine (PAAG15A) for cystic fibrosis treatment. PAAG15A is being developed by Synspira as as SNSP113, an investigational inhaled treatment to boost lung function in cystic fibrosis patients by targeting the key drivers of pulmonary decline, […]
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